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Medicine
fromArs Technica
1 day ago

Bad cholesterol slashed 62% by single dose of gene-editing drug in small trial

VERVE-102 uses base editing to permanently disrupt PCSK9, reducing LDL in a dose-dependent manner with larger doses producing greater gene knockout and LDL lowering.
Medicine
fromThe Washington Post
3 months ago

David Liu unlocks the power of gene editing to treat rare genetic diseases

Base and prime gene-editing technologies can precisely correct genetic mutations, enabling personalized therapies that can cure life-threatening inherited diseases.
Medicine
fromwww.bbc.com
5 months ago

Pioneering new treatment reverses incurable blood cancer in some patients

Base editing of patients' white blood cells can reverse aggressive, treatment-resistant T-cell acute lymphoblastic leukaemia, achieving remission in about 64% of treated cases.
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Medicine
fromwww.nature.com
6 months ago

Gene Editing Helped One BabyCould It Help Thousands?

Personalized base-editing therapy cured baby KJ; a clinical trial plans to deliver multiple similarly tailored treatments faster after negotiating simplified regulatory pathways.
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