Northern Minnesota boy is first American to receive groundbreaking treatment for muscular dystrophyColton Belluzzo received groundbreaking gene therapy for Duchenne muscular dystrophy, showing promise in slowing disease progression.
Patient dies following muscular dystrophy gene therapy, Sarepta reportsA patient died from acute liver injury while using Sarepta's Elevidys gene therapy for muscular dystrophy, causing a major stock market reaction.
Young Patient Dies After Receiving Pfizer Gene TherapyThe tragic death of a young boy during a Pfizer medical trial for Duchenne muscular dystrophy has raised concerns and questions among scientists and parents.
Minneapolis parents share journey of having two sons with rare muscle-wasting disorderThe Kasner family faces Duchenne muscular dystrophy with resilience and a strong support network, embracing love and life despite the challenges.
Northern Minnesota boy is first American to receive groundbreaking treatment for muscular dystrophyColton Belluzzo received groundbreaking gene therapy for Duchenne muscular dystrophy, showing promise in slowing disease progression.
Patient dies following muscular dystrophy gene therapy, Sarepta reportsA patient died from acute liver injury while using Sarepta's Elevidys gene therapy for muscular dystrophy, causing a major stock market reaction.
Young Patient Dies After Receiving Pfizer Gene TherapyThe tragic death of a young boy during a Pfizer medical trial for Duchenne muscular dystrophy has raised concerns and questions among scientists and parents.
Minneapolis parents share journey of having two sons with rare muscle-wasting disorderThe Kasner family faces Duchenne muscular dystrophy with resilience and a strong support network, embracing love and life despite the challenges.
Doctors Said These Women's Mutated Genes Wouldn't Harm ThemGenetic screening during IVF can lead to difficult choices regarding embryo selection and raises questions on medical understanding of X-linked diseases.
Transcriptional adaptation upregulates utrophin in Duchenne muscular dystrophy - NatureUtrophin upregulation serves as a compensatory mechanism in DMD, linked to a newly identified process called transcriptional adaptation.
Doctors Said These Women's Mutated Genes Wouldn't Harm ThemGenetic screening during IVF can lead to difficult choices regarding embryo selection and raises questions on medical understanding of X-linked diseases.
Transcriptional adaptation upregulates utrophin in Duchenne muscular dystrophy - NatureUtrophin upregulation serves as a compensatory mechanism in DMD, linked to a newly identified process called transcriptional adaptation.
Twin boys living with muscle-wasting disease given hope after invitation to clinical trial in USTwins George and Isaac Naughton are seeking help to travel to the US for treatment of Duchenne Muscular Dystrophy.