#huntingtons-disease

#huntingtons-disease

I've never cared much for Thanksgiving. As a child, the forced family gathering was tolerable only because it marked the halfway point to Christmas (if we are measuring from Halloween, which is what we do in holiday math). As an adult, I came to understand some of the complications in celebrating a holiday with such a (distinctly American) white-washed backstory.

But last Wednesday was a day unlike any other. I cried with every single patient, Sung says. It just was this crazy feeling that, for the patients and families, almost can't feel real. That day the results of important phase 1/2 clinical trials had finally been released: an experimental gene therapy drug was the first treatment shown to slow the progression of Huntington's disease.

Family say they were left in dark about risk of them developing the neurodegenerative disorder